List of gene therapies
This article contains a list of commercially available gene therapies.
Gene therapies[]
- Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available?)
- Axicabtagene ciloleucel: treatment for large B-cell lymphoma
- Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia
- Brexucabtagene autoleucel (Tecartus): treatment for mantle cell lymphoma and acute lymphoblastic leukemia[1][2]
- Cambiogenplasmid: treatment for vascular endothelial growth factor peripheral artery disease
- Elivaldogene autotemcel (Skysona): treatment for cerebral adrenoleukodystrophy
- Gendicine: treatment for head and neck squamous cell carcinoma
- Onasemnogene abeparvovec (Zolgensma): AAV-based treatment for spinal muscular atrophy
- Resamirigene bilparvovec: AAV-based experimental therapy for X-linked myotubular myopathy
- Strimvelis: treatment for adenosine deaminase deficiency (ADA-SCID)
- Talimogene laherparepvec: treatment for melanoma in patients who have recurring skin lesions
- Tisagenlecleucel: treatment for B cell lymphoblastic leukemia
- Voretigene neparvovec (Luxturna): AAV-based treatment for Leber congenital amaurosis
See also[]
References[]
- ^ "FDA Approves First Cell-Based Gene Therapy For Adult Patients with Relapsed or Refractory MCL". U.S. Food and Drug Administration (FDA). 24 July 2020. Retrieved 24 July 2020.
- ^ "FDA approves brexucabtagene autoleucel for relapsed or refractory B-cell precursor acute lymphoblastic leukemia". U.S. Food and Drug Administration (FDA). 1 October 2021. Retrieved 2 October 2021.
- Daley, Jim (1 January 2020). "Gene Therapy Arrives". Scientific American. Retrieved 9 June 2020.
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Categories:
- Gene therapy
- Applied genetics
- Bioethics
- Biotechnology
- Medical genetics
- Molecular-biology-related lists
- Gene delivery
- Emerging technologies
- Genetic engineering